Innovating Works

GOSH

Desconocido
PHEMS: Pediatric Hospitals as European drivers for multi-party computation and synthetic data generation ca... GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un HORIZON EUROPE: HORIZON-HLTH-2022-IND-13 Cross-border collaboration can tackle the challenges in accessing relevant health data essential for international collaboration between sci...
2023-10-09 - 2026-09-30 | Financiado
BIND: Brain Involvement iN Dystrophinopathies GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un H2020: H2020-SC1-BHC-2018-2020 Duchenne muscular dystrophy (DMD) is the most common muscular dystrophy in childhood, with more than 25,000 patients in Europe. It is due to...
2019-12-05 - 2024-06-30 | Financiado
RECOMB: Stem cell based gene therapy for recombination deficient SCID RECOMB GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un H2020: H2020-SC1-2016-2017 Gene therapy for rare inherited immune disorders has become a clinical reality. Especially for SCID, two major types of SCID (ADA-SCID, X-SC...
2017-11-21 - 2024-12-31 | Financiado
SCIDNET: DevelopIng Genetic medicines for Severe Combined Immunodeficiency SCID GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un H2020: H2020-PHC-2014-2015 Severe combined immunodeficiency (SCID) is a devastating rare disorder of immune system development. Affected infants are born without funct...
2015-12-02 - 2019-12-31 | Financiado
BOOSTB4: Boost Brittle Bones Before Birth GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un H2020: H2020-PHC-2014-2015 Osteogenesis imperfecta (OI) is, in its severe forms, a devastating inherited disorder characterised by brittle bones. A person with severe...
2015-09-11 - 2022-12-31 | Financiado
BETACURE: Personalized diagnosis and treatment of hyperinsulinemic hypoglycaemia caused by beta cell pathology GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un FP7: Background: Hyperinsulinaemic hypoglycaemia (HH) is a potentially lethal disease caused by over functioning beta cells derived from the panc...
Financiado
PANCARESURFUP: PanCare Childhood and Adolescent Cancer Survivor Care and Follow up Studies GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un FP7: Over the last 40 years, treatment for childhood and adolescent cancer has improved greatly; 5- year survival after childhood cancer is now 8...
Financiado
LENA: Labeling of Enalapril from Neonates up to Adolescents GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un FP7: Children are often treated as small adults—not as the special patients they are. Regulations exist to encourage the development of drugs and...
Financiado
EUNEFRON: European Network for the Study of Orphan Nephropathies GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un FP7: In this proposal, we have mobilized a critical mass of expertise to investigate, on a Europe-wide scale, the natural history and pathophysio...
Financiado
ESPOIR: European clinical study for the application of regenerative heart valves GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un FP7: Acquired and congenital heart disease can necessitate heart valve replacement. However, current heart valve substitutes are not considered i...
Financiado
NEMO: Treatment of NEonatal seizures with Medication Off patent evaluation of efficacy and safety of bume... GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un FP7: Neonatal hypoxic ischaemic encephalopathy (HIE) occurs in 2-3/1000 live births and is a major cause of both acute mortality and long-term ne...
Financiado
STOP: Suicidality Treatment Occurring in Paediatrics GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un FP7: The emergence of suicidality in patients receiving drug treatment is of concern because of the overall burden and the possible link with com...
Financiado
SKIP-NMD: A phase I IIa clinical trial in Duchenne muscular dystrophy using systemically delivered morpholino... GREAT ORMOND STREET HOSPITAL FOR CHILDREN NHS FOUNDATION TRUST participó en un FP7: Duchenne muscular dystrophy (DMD) is a progressive, lethal muscle degenerative condition arising from the absence of dystrophin in skeletal...
Financiado
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