Innovating Works

WWOXAID

Financiado
A Promising Treatment of WWOX Associated Neurological Disorders
A Promising Treatment of WWOX Associated Neurological Disorders WWOXAID WWOX-related epileptic encephalopathy (WOREE) syndrome, also known as early infantile epileptic encephalopathy, 28 (EIEE28, OMIM: 616211), is a very severe e... A Promising Treatment of WWOX Associated Neurological Disorders WWOXAID WWOX-related epileptic encephalopathy (WOREE) syndrome, also known as early infantile epileptic encephalopathy, 28 (EIEE28, OMIM: 616211), is a very severe epileptic encephalopathy characterized by absence of language development and acquisition of walking, early-onset drug-resistant seizures, ophthalmological involvement, and a very high likelihood of premature death. Above all, WWOXAID aims to set the basis for bringing into clinical development a treatment for WOREE syndrome affecting children in infancy. Although WOREE syndrome has very limited market prospects, since the number of known patients is low and no current active registry is available, this development is critical because there is no current treatment that could save children with WOREE. In addition to this highly humanitarian purpose, we are confident that this PoC achievement shall be also of importance for broadening the spectrum of applications of this treatment in other WWOX-related disorders. In this PoC, we will achieve several necessary steps including the generation, characterization and delivery of the vectors, securing IPRs, conducting a specific market assessment, targeting regulatory constraints, implementing a business development plan, consulting with professionals in the field and developing contacts with the industry, dedicated organizations and medical doctors. ver más
31/01/2022
THE HEBREW UNIVERS...
150K€
Duración del proyecto: 18 meses Fecha Inicio: 2020-07-15
Fecha Fin: 2022-01-31

Línea de financiación: concedida

El organismo H2020 notifico la concesión del proyecto el día 2022-01-31
Línea de financiación objetivo El proyecto se financió a través de la siguiente ayuda:
ERC-2020-POC: Call for proposals for ERC Proof of Concept Grant
Cerrada hace 4 años
Presupuesto El presupuesto total del proyecto asciende a 150K€
Líder del proyecto
THE HEBREW UNIVERSITY OF JERUSALEM No se ha especificado una descripción o un objeto social para esta compañía.
Perfil tecnológico TRL 4-5